@article{WalterReilichThieleetal.2013, author = {Maggie C. Walter and Peter Reilich and Simone Thiele and Joachim Schessl and Herbert Schreiber and Karlheinz Reiners and Wolfram Kress and Clemens M{\"u}ller-Reible and Matthias Vorgerd and Peter Urban and Bertold Schrank and Marcus Deschauer and Beate Schlotter-Weigel and Ralf Kohnen and Hans Lochm{\"u}ller}, title = {Treatment of dysferlinopathy with deflazacort: a double-blind, placebo-controlled clinical trial}, journal = {Orphanet Journal of Rare Diseases}, volume = {8}, number = {26}, doi = {10.1186/1750-1172-8-26}, year = {2013}, }